Transfer of genetic therapy across human populations: Molecular targets for increasing patient coverage in repeat expansion diseases

  1. Varela, M.A.
  2. Curtis, H.J.
  3. Douglas, A.G.L.
  4. Hammond, S.M.
  5. O'Loughlin, A.J.
  6. Sobrido, M.J.
  7. Scholefield, J.
  8. Wood, M.J.A.
Journal:
European Journal of Human Genetics

ISSN: 1476-5438 1018-4813

Year of publication: 2016

Volume: 24

Issue: 2

Pages: 271-276

Type: Article

DOI: 10.1038/EJHG.2015.94 GOOGLE SCHOLAR lock_openOpen access editor