The effect of enzyme replacement therapy on clinical outcomes in paediatric patients with Fabry disease – A systematic literature review by a European panel of experts

  1. Spada, M.
  2. Baron, R.
  3. Elliott, P.M.
  4. Falissard, B.
  5. Hilz, M.J.
  6. Monserrat, L.
  7. Tøndel, C.
  8. Tylki-Szymańska, A.
  9. Wanner, C.
  10. Germain, D.P.
Journal:
Molecular Genetics and Metabolism

ISSN: 1096-7206 1096-7192

Year of publication: 2019

Volume: 126

Issue: 3

Pages: 212-223

Type: Review

DOI: 10.1016/J.YMGME.2018.04.007 GOOGLE SCHOLAR lock_openOpen access editor