The effect of enzyme replacement therapy on clinical outcomes in paediatric patients with Fabry disease – A systematic literature review by a European panel of experts
- Spada, M.
- Baron, R.
- Elliott, P.M.
- Falissard, B.
- Hilz, M.J.
- Monserrat, L.
- Tøndel, C.
- Tylki-Szymańska, A.
- Wanner, C.
- Germain, D.P.
ISSN: 1096-7206, 1096-7192
Ano de publicación: 2019
Volume: 126
Número: 3
Páxinas: 212-223
Tipo: Revisión